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Transplant Outcomes in Children with Fanconi anaemia

Severe Aplastic Anaemia Working Party (SAAWP)
Paediatric Diseases Working Party (PDWP)
Study number:
8409081
Short title:
 
Study status:
 
Deadline for data collection:
 
Study design:
Retrospective study design
Primary objective:
To study the outcomes in children with FA who were transplanted from 2010 to 2018
Key inclusion criteria:
Inclusion criteria:
1. All patients with FA who underwent first HSCT
2. HSCT from 2010-2018
3. Age ≤18 years at time of HSCT
4. All indications: bone marrow failure, myelodysplasia, acute leukaemia
5. All donor types: matched family/sibling donor, matched unrelated donor, mismatched family/unrelated donor, haploidentical donor
Country:
 
Principal investigator:
Su Han Lum, Sujith Samarasinghe
Principal investigator email:
s.lum@nhs.net
EBMT Study coordinator:
Arnaud Dalissier
Study coordinator email:
arnaud.dalissier@upmc.fr