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Transplant Outcomes in Children with Fanconi anaemia

Severe Aplastic Anaemia Working Party (SAAWP)
Paediatric Diseases Working Party (PDWP)
Study type:
Study number:
Type of Stem Cell Treatment:
Bone marrow failure
Short title:
Primary objective:
To study the outcomes in children with FA who were transplanted from 2010 to 2018
Key inclusion criteria:
Inclusion criteria:
1. All patients with FA who underwent first HSCT
2. HSCT from 2010-2018
3. Age ≤18 years at time of HSCT
4. All indications: bone marrow failure, myelodysplasia, acute leukaemia
5. All donor types: matched family/sibling donor, matched unrelated donor, mismatched family/unrelated donor, haploidentical donor
Principal investigator:
Su Han Lum, Sujith Samarasinghe
EBMT Study coordinator:
Arnaud Dalissier
Study coordinator email: