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Androgens in bone marrow failure disorders

Severe Aplastic Anaemia Working Party (SAAWP)
Study number:
Type of Stem Cell Treatment:
Short title:
Androgens in bone marrow failure disorders
Primary objective:
To evaluate the use of androgens in BMF disorders in EBMT centers
Key inclusion criteria:
1) Diagnosis with an inherited or acquired BMF between 2000 and 2019;
2) Androgen-based treatment along patient's disease course, before or in the absence of allogeneic HSCT;
3) Patients of all ages.

Exclusion criterium: All patients receiving a transplant before androgen’s use do not qualify for this study.
Principal investigator:
Simona Pagliuca, Austin Kulasekararaj
EBMT Study coordinator:
Brian Piepenbroek
Study coordinator email: