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Outcomes of allogeneic stem cell transplantation in paediatric patients affected with autosomal dominant RUNX1 mutation related disease

Paediatric Diseases Working Party (PDWP)
Study type:
Study number:
 
Type of Stem Cell Treatment:
 
Diseases:
 
Short title:
 
Primary objective:
Collaboration EWOG EBMT and some UK centers
Key inclusion criteria:
Patients affected with autosomal dominant RUNX1 mutation related disease
Country:
 
Principal investigator:
Giovanna Lucchini
EBMT Study coordinator:
Arnaud Dalissier
Study coordinator email:
arnaud.dalissier@upmc.fr