Top Back to top

HSCT for Congenital Amegakaryocitic thrombopecytopenia (CAMT)

Paediatric Diseases Working Party (PDWP)
Type d'étude:
Numéro de l'étude:
8417036
Type de traitement à base de cellules souches:
Allogeneic
Maladies:
Bone marrow failure
Titre court:
CAMT study
Objectif principal:
Primary Aim: The aim is to evaluate outcomes of paediatric patients with congenial amegakaryocytic thrombocytopenia.
Principaux critères d'inclusion:
• Age at TX < 18years
• First allogeneic transplant
• Diagnosis: Congenial amegakaryocytic thrombocytopenia
• Year of inclusion: Until 2019 (included
Pays:
 
Investigateur principal:
Clémence Aldebert
Coordinateur EBMT de l'étude:
Arnaud Dalissier
E-mail du coordinateur de l'étude:
arnaud.dalissier@upmc.fr