Inborn Errors Working Party (IEWP)
Study type:
Study number:
Type of Stem Cell Treatment:
Diseases:
Short title:
Primary objective:
Key inclusion criteria:
Inclusion criteria: all cord blood transplanted patients for inherited metabolic diseases between 1.1.2004-31.12.2016
Country:
Principal investigator:
Su Han Lum
EBMT Study coordinator:
Henric-Jan Blok
Study coordinator email:
iewpebmt@lumc.nl