Inborn Errors Working Party (IEWP)
Study type:
Study number:
8427015
Type of Stem Cell Treatment:
Allogeneic
Diseases:
Short title:
ICF syndrome
Primary objective:
Key inclusion criteria:
ICF syndrome patients (all ages; genetically confirmed or strong clinical suspicion) that have undergone HSCT.
Country:
Principal investigator:
Dagmar Berghuis
EBMT Study coordinator:
Sheree Hazelaar/ Jorinde Hoogenboom
Study coordinator email:
iewpebmt@lumc.nl