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Haematopoietic stem cell transplantation in lysosomal acid lipase deficiency (Wolman Disease): A survey from Inborn Errors Working Party of EBMT

Inborn Errors Working Party (IEWP)
Study type:
Retrospective Studies
Study number:
 
Type of Stem Cell Treatment:
Allogeneic
Diseases:
 
Short title:
 
Primary objective:
 
Key inclusion criteria:
all patients transplanted for Wolman Disease
Country:
 
Principal investigator:
Su Han Lum
EBMT Study coordinator:
Henric-Jan Blok
Study coordinator email:
iewpebmt@lumc.nl